Enzerna Biosciences Inc
Enzerna Biosciences Inc. is a pre-clinical stage company based in Greenville, NC, dedicated to developing long-term curative gene therapies for rare genetic disorders. Leveraging their proprietary RNA editing technology, they are pioneering gene therapies for nucleotide expansion disorders such as Myotonic Dystrophy and Huntington's Disease, targeting the root cause of these diseases by destroying the disease-causing RNA molecules using Artificial Site-Specific RNA Endonucleases (ASREs).
Enzerna's ASRE technology, which specifically targets disease-causing nucleotide repeats at the RNA level, sets it apart from other DNA modifying technologies like CRISPR Cas. With a focus on developing innovative therapeutic strategies, Enzerna Biosciences Inc. aims to provide hope and potential long-term solutions for patients suffering from these debilitating genetic disorders.
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