Spinal Muscular Atrophy

The Spinal Muscular Atrophy Foundation is a non-profit organization based in New York, NY, dedicated to expediting the development of treatments for Spinal Muscular Atrophy (SMA), the leading genetic cause of death in young children. With 1 in 50 people being carriers of the disease, the foundation aims to raise awareness and support research efforts to combat SMA. They have successfully facilitated the approval of three FDA drugs and continue to drive clinical trials for further advancements.

The foundation recently mourned the loss of Steve Mikita, a valued member of their board of directors, highlighting their commitment to the cause and the personal connections they foster within their organization. As they strive to make a difference in the lives of those affected by SMA, the Spinal Muscular Atrophy Foundation remains dedicated to their mission of accelerating treatment development and improving outcomes for individuals with this debilitating condition.

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